Pre-Clinical Stage In-Silico Complete CDA/NDA Required

Engineering Structural Neuroplasticity via
Targeted 5-HT2A Modulation

SynaptiCore Therapeutics is advancing a non-hallucinogenic indole derivative. Designed to selectively restore synaptic density, our candidate aims to address synaptic atrophy underlying complex neurodegenerative conditions.

This page summarizes computational parameters prior to wet-lab synthesis. SMILES notation and synthetic routes are strictly confidential under Mutual NDA.

In-Silico Profile — Lead Candidate SC-01
Target Engagement Highly Predicted (In-Silico)
Lipinski Ro5 Compliance 0 Violations
BBB Permeability High (Predicted)
Synthetic Accessibility Favorable (SA: ~2.5)
Toxicity Endpoint (ProTox-II) Mutagenicity Inactive
Current Status Lead Candidate Selected
Computational Data Profiling Completed
Wet-Lab Validation Seeking CRO Partners
Scientific Rationale

A Data-Driven Approach to Neural Repair

Background & Rationale

The objective of SynaptiCore Therapeutics is structural disease modification. Current psychiatric and neurodegenerative treatments often act as temporary symptom management. By focusing on structural neuroplasticity, we aim to address the physical atrophy of dendritic spines.

In-silico molecular docking was performed against the 5-HT2A receptor (PDB: 6WHA), demonstrating favorable binding kinetics and fulfilling Lipinski's parameters via SwissADME. By computationally refining a known neurotrophic core, we engineered SC-01: a modified indole scaffold designed for optimal BBB penetration and targeted receptor engagement, without the hallucinogenic liability.

Restorative Synaptogenesis

Our targeted approach aims to stimulate intracellular pathways (such as mTOR) to restore mature, functional connections in atrophied neural networks.

Fluorinated Core (OCF3)

SC-01 utilizes a strategically modified indole scaffold. By introducing a trifluoromethoxy (OCF3) substitution, we successfully elevated predicted lipophilicity for BBB crossing while protecting the core from metabolic degradation.

Controlled Signaling

Computational docking (via PyRx/AutoDock Vina) confirms stable, high-affinity interaction with the orthosteric site, allowing us to predict powerful target engagement prior to in-vitro assays.

Structural Details Withheld

Detailed synthetic routes, exact receptor docking poses, and precise scaffold modifications are protected intellectual property.

Request Information via NDA
CRO Engagement Roadmap

Transitioning to Wet-Lab

SynaptiCore has successfully completed the computational evaluation phase. We are actively engaging Contract Research Organizations (CROs) via Science Exchange to execute the physical synthesis and validate the in-vitro efficacy of our lead compound.

Synthetic Considerations: While the in-silico profile is highly favorable (SA Score: ~2.5), we anticipate standard challenges in the multi-step custom synthesis, particularly regarding intermediate purification and potential steric hindrance around the trifluoromethoxy (OCF3) substitution. We are seeking CRO partners equipped to navigate these specific synthetic hurdles.

Requested CRO Pipeline

We are seeking proposals for the following sequence:

  • Phase 1: Custom Synthesis (Route scouting, overcoming steric constraints, initial ~10-50mg batch, >95% purity via HPLC/NMR)
  • Phase 2: Safety & Toxicity (MTT cytotoxicity assay & Ames test)
  • Phase 3: Efficacy In-Vitro (Dendritic spine quantification in cortical neurons)
SC-01 · Pre-Clinical Data Highlights
SWISSADME PROFILING
GI Absorption High
BBB Permeant Yes
Lipinski Violations 0
PROTOX-II TOXICITY PREDICTION
Hepatotoxicity Risk Inactive
Mutagenicity Risk Inactive
SYNTHESIS PARAMETERS
Target Purity / Scale > 95% / 10-50mg
Synthetic Accessibility ~2.5 (Favorable)